bibliographic resource 2726612 [br/2726612]
https://w3id.org/oc/corpus/br/2726612

is a
title
  • Safety and pharmacodynamic effects of a pharmacological chaperone on α-galactosidase A activity and globotriaosylceramide clearance in Fabry disease: report from two phase 2 clinical studies
publication date
  • 2012-01-01
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